3 results
Approved WMORecruiting
the objective of the current study is to evaluate the safety and efficacy of enzyme therapy in the Dutch population of patients with MPS I, II and VI; to compare this to the natural course of these diseases; to make an inventory of the direct and…
Approved WMOCompleted
The main objective of this trial is to investigate safety of long term use of inhaled molgramostim by collecting information on the side effects.
Approved WMOWill not start
The main objective of this trial is to investigate the efficacy of inhaled molgramostim compared to placebo.