2 results
Approved WMORecruiting
Primary:To compare the efficacy of asciminib versus Investigator selected TKI with respect to the proportion of patients that are in Major Molecular Response at Week 48. To compare the efficacy of asciminib versus Investigator selected TKI, within…
Approved WMORecruiting
Primary objective:To assess the long term safety and tolerability of GIVINOSTAT in patients with DMD following core protocols program and with naïve GIVINOSTAT DMD subjects , i.e. subjects screened in study DSC/14/2357/48 who met:- all the inclusion…