2 results
Approved WMOPending
The overall objective is to assess efficacy, safety, pharmacokinetic (PK), pharmacodynamics (PD) of avalglucosidase alfa in male and femaleparticipants less than or equal to 6 months of age with IOPD.
Approved WMOCompleted
Long-term safety and pharmacokinetics (PK) of neoGAA