2 results
Approved WMOCompleted
Primary Objective(s): To evaluate long-term safety in patients with mucopolysaccharidosis type IIIA disease (MPS IIIA or Sanfilippo Type A) who received HGT-1410Secondary Objective(s):To evaluate:• The long-term cognitive function as measured by the…
Approved WMOCompleted
The primary objective is to show that the ORION SYSTEM is safe and performs as intended.