3 results
Approved WMOCompleted
Primary purpose: study the feasibility of a new treatment option based on biofeedback in people with intellectual disabilities.Secondary purpose: explore effects of treatment for swallowing problems in people with intellectual disabilities.
Approved WMOCompleted
The overall objective of this study is to evaluate the efficacy and safety of neoGAA in treatment-naïve patients with LOPD as compared to alglucosidase alfa, when this is administered biweekly for a period of 49 weeks. Also, there is an open-label…
Approved WMOCompleted
The objective of the study is to assess the safety, tolerability and efficacy of PRO044.