2 results
Approved WMORecruiting
The primary objectives are: To evaluate the CNS activity of DNL310 vs idursulfase as measured by the cerebrospinal fluid (CSF) concentration of heparan sulfate (HS) in participants with the neuronopathic form of mucopolysaccharidosis type II (nMPS…
Approved WMORecruiting
To compare the progression free survival and neurotoxity of first line treatment with F-Nal-IRI, CapCar and CapOx.