2 results
A Multicenter, Open-Label Study of Sebelipase Alfa in Patients with Lysosomal Acid Lipase deficiency
The primary objective of this study is to evaluate the safety of sebelipase alfa in a more broad population of subjects with LAL Deficiency than have been previously studied.The secondary objectives of this study are (1) to evaluate effects of…
Approved WMOCompleted
The main objective of this study is to find if there is a measurable improvement of transfemoral amputees standing up with the active knee support prosthesis (ERK) in comparison to standing up without active knee support.