4 results
The main objective of this trial is to investigate safety of long term use of inhaled molgramostim by collecting information on the side effects.
To obtain histopathology from liver lesions, visible on MRI but which cannot be biopsied with transabdominal ultrasound, using MR-guided biopsy.
Primary objective:* To establish the effects of givinostat versus placebo administered chronically over 18 months to slow disease progression in ambulant DMD subjects.Secondary objectives:* To assess the safety and tolerability of givinostat versus…
The primary objective of the present study is to establish the histological effects of givinostat versus placebo administered over 12 months. The secondary objectives of this study are the following: - To establish the macroscopic muscle effects of…