3 results
Approved WMOCompleted
The purpose of this trial is primarily to assess the efficacy of inhaled mannitol compared with a true placebo in subjects with cystic fibrosis aged 6 to 17 years.We hypothesize that inhaled mannitol will improve the overall health and hygiene of…
Not approvedWill not start
This pilot clinical trial has been designed to evaluate the safety and performance of the INSTRUCT scaffold, and to collect preliminary efficacy data
Approved WMORecruiting
To study the safety and efficacy of mitapivat in the treatment of adult subjects with sickle cell disease.