2 results
Approved WMORecruiting
Part A: Safety:• To characterize the safety and tolerability of up to four dose levels of rilzabrutinibin patients with ITPEfficacy:• To explore the clinical activity of up to four dose levels of rilzabrutinibin relapsed/refractory patients with ITP…
Approved WMORecruiting
Assess the potential efficay of L-serine dietary supplementation in patients children with a GRIN2B LoS mutation.