2 results
Approved WMOCompleted
To study whether hyqvia is as effective, safe and tolerable (or more tolerable) as IVIg.
Approved WMOCompleted
The objective of this pivotal study is to assess the long-term safety, tolerability, pharmacokinetics and pharmacodynamics of RP103 in pediatric and adult patients with nephropathic cystinosis. Results of this Phase 3 study will be used to support…