4 results
To determine the safety and efficacy of coversin in the treatment of patients with PNH resistant to eculizumab.
Studying the effect of deferiprone on the motor function of patients with Pelizaeus-Merzbacher disease.
Objectives The main objective of the FAIR-PARK II trial is to demonstrate an effect of DFP on the course of PD (including both disease-modifying and symptomatic effects). The trial's overall objective can be summarized as follows: to…
* The purpose of this study is to to determine the safety profile of long-termCoversin treatment.* To observe the long term safety and efficacy of Coversin over periods in excess of 6 months* To assess the long term patient acceptability of Coversin…