4 results
Approved WMOCompleted
To investigate the effect of cholic acid supplementation on the clinical and biochemical parameters of Zellweger spectrum disorder
Approved WMOPending
To evaluate the efficacy of crovalimab compared to eculizumab
Approved WMOPending
To evaluate the safety and tolerability of crovalimab compared witheculizumab
Approved WMORecruiting
Investigating the long-term safety of personalized cholic acid treatment in patients with defects in bile acid synthesis based on clinical and biochemical parameters.