2 results
Approved WMOCompleted
The aim of this study is to investigate 1. the extent to which patients who have paresis/non-spastic paralysis of the lower extremity and who are moderately active experience an improvement in the (trunk) balance through the use of a computer-…
Approved WMOCompleted
Primary objectives: 1. To compare the efficacy of vamorolone administered orally at daily doses of 6.0 mg/kg over a 24-week treatment period vs. placebo in ambulant boys ages 4 to <7 years with DMD; and2. To evaluate the safety and…