2 results
Approved WMOPending
Assess the neurological efficacy of ambroxol in adults and children with GD3.
Approved WMORecruiting
OBJECTIVES - Phase 2 (not to be conducted in NL):Phase 2 Primary Objective:- Identify a setrusumab dosing strategy in subjects with OI Phase 2 Secondary Objectives:- Evaluate the PK of setrusumab doses in subjects with OI- Determine the PD effects…