2 results
Approved WMOPending
Assess the neurological efficacy of ambroxol in adults and children with GD3.
Approved WMOCompleted
Primary: The primary objective of the study is to evaluate the long-term safety of rFIXFc in subjects with hemophilia B.Secondary: The secondary objective of this study is to evaluate the efficacy of rFIXFc in the prevention and treatment of…