3 results
Approved WMOCompleted
The primary objective of the study is to evaluate the safety, tolerability, PK, and PD of AL002 administered in single ascending doses in healthy participants and multiple doses in participants with mild to moderate AD.
Approved WMORecruiting
1. To report the natural history of retinal degeneration in patients with biallelic mutations in the EYS gene.2. To identify sensitive structural and functional outcome measures to use for future multicenter clinical trials in EYS-related retinal…
Approved WMOPending
To evaluate the efficacy of AL002 in participants with Early AD in delaying disease progression compared to standard of care