3 results
Primary: To assess the efficacy of intracerebral delivery of AAVrh.10SGSH gene therapy (LYS-SAF302) in improving or stabilizing the neurodevelopmental status of MPS IIIA patients after 24 months (main cohort), compared to the expected evolution…
Primary objective: To evaluate the performance of the SCP procedure in treatment of bone marrow lesion(s) (BML(s)).Secondary objective:Secondary objectives include documenting clinical outcomes such as pain, function of daily living, function of…
to demonstrate that the ProSpace, when properly inserted between the prostate and the rectum is safe and effective in reducing the volume of the rectum receiving greater or equal to 70 Gy (VRectum70) by means of IMRT in prostate cancer patients…