2 results
Approved WMORecruiting
The objective of the study is to evaluate the safety and performance of a new Non-Invasive Ultrasound Therapy (NIUT) with Valvosoft® in the treatment of CAS.
Approved WMOCompleted
To demonstrate the efficacy of repeated daily doses of 40 µg/kg/day and 120 µg/kg/day A4250 in children with progressive familial intrahepatic cholestasis (PFIC) Types 1 and 2, as determined by the following:* Proportion of patients experiencing at…