2 results
Approved WMOCompleted
To demonstrate the efficacy of repeated daily doses of 40 µg/kg/day and 120 µg/kg/day A4250 in children with progressive familial intrahepatic cholestasis (PFIC) Types 1 and 2, as determined by the following:* Proportion of patients experiencing at…
Approved WMOPending
By performing this study, in case the results are positive (SMS images are equally diagnostic as compared to current imaging techniques), the SMS sequence can be implemented in standard clinical care for patients referred for cardiac MRI, reducing…