3 results
Approved WMOCompleted
Primary Objective• To evaluate the efficacy of two dosage regimens of palovarotene compared with placebo in preventing new osteochondromas (OCs) in subjects with multiple osteochondromas (MO) due to exostosin 1 (Ext1) or exostosin 2 (Ext2) mutations…
Approved WMOWill not start
The primary aim of this study is to examine the feasibility, usability, and acceptability of the educational care pathway for both patients and healthcare professionals. The secondary aim is to investigate the preliminary effects on patients*…
Approved WMOCompleted
To evaluate the effect of Obeticholic Acid on clinical outcomes in subjects with primary biliary cholangitis