3 results
Approved WMOCompleted
The objectives of the study are to evaluate the following in patients with a documented history of EPP:•determine whether CUV1647 can reduce the number of phototoxic reactions in patients with EPP•determine whether CUV1647 can reduce the severity of…
Not approvedWill not start
This pilot clinical trial has been designed to evaluate the safety and performance of the INSTRUCT scaffold, and to collect preliminary efficacy data
Approved WMORecruiting
To study the safety and efficacy of mitapivat in the treatment of adult subjects with sickle cell disease.