3 results
Approved WMOCompleted
The primary objective of TRIHEP 3 is to evaluate the efficacy of triheptanoin in (i) increasing the short term energy response in the metabolic profile of the brain of early affected HD patients, as captured by 31P-MRS, and (ii) slowing atrophy in…
Approved WMOCompleted
Main objective: To assess the effect of CK-2127107 versus placebo on respiratory function in patients with ALS.
Approved WMOCompleted
To generate high quality empirical evidence for the effectiveness in terms of proportion of patients experiencing complications, quality of life and costs of initial non-operative treatment strategy (reserving appendectomies for those not responding…