2 results
Approved WMOCompleted
The objectives of the study are:* To evaluate the safety and tolerability of zilucoplan in subjects with IMNM* To evaluate the efficacy of zilucoplan in subjects with IMNM
Approved WMOPending
To evaluate the effects of N-acetylcysteine (NAC; FluimucilĀ® in Dutch) on skin picking behaviour in children and young adults with PWS.