2 results
Approved WMOCompleted
The primary objective is to assess the long-term safety and tolerability of tirasemtiv, inpatients with ALS
Approved WMOWill not start
To characterize the PK of eltrombopag at steady state after oral administration in pediatric patients with SAA.Secondary (key only, see protocol page 40-41 for all objectives): Safety and tolerability. Efficacy (overall response rate ORR).