5 results
To investigate the effect of cholic acid supplementation on the clinical and biochemical parameters of Zellweger spectrum disorder
This study will evaluate the efficacy and safety of multiple therapies that are selected using somatic alterations and potential predictive biomarkers identified via NGS assays in patients with solid tumors.
The main objective is to study the efficacy of treatment with RTX in patients with relapsing PMR compared to placebo.
The main objective is to study the efficacy of treatment with RTX in patients with newly diagnosed PMR compared to placebo.
Investigating the long-term safety of personalized cholic acid treatment in patients with defects in bile acid synthesis based on clinical and biochemical parameters.