4 results
Approved WMOCompleted
To investigate the effect of cholic acid supplementation on the clinical and biochemical parameters of Zellweger spectrum disorder
Approved WMORecruiting
The main objective is to study the efficacy of treatment with RTX in patients with relapsing PMR compared to placebo.
Approved WMORecruiting
The main objective is to study the efficacy of treatment with RTX in patients with newly diagnosed PMR compared to placebo.
Approved WMORecruiting
Investigating the long-term safety of personalized cholic acid treatment in patients with defects in bile acid synthesis based on clinical and biochemical parameters.