2 results
Approved WMOPending
Assess the neurological efficacy of ambroxol in adults and children with GD3.
Not approvedWill not start
Primary Objective:Double-blind period : Evaluate the effect of SRP-4045 and SRP-4053 (combined-active group) compared to placebo on ambulation, endurance, and muscle function, as measured by the 6MWTSecondary Objectives:- Double-blind period:…